Treatment of ADA-SCID is often considered the first success for gene therapy. Ashanti DeSilva is a young girl that suffered from an autosomal form of SCID and was treated using retroviral gene therapy. Explain why the treatment is not an undisputed

success.

What will be an ideal response?


While Ashanti's immune system was bolstered by the gene therapy, she also received regular injections of adenosine deaminase enzyme. This made it unclear whether the adenosine deaminase found in her system was due to the active gene delivered by the gene therapy or the injections of purified adenosine deaminase.

Biology & Microbiology

You might also like to view...

What is a primary difference between polymerase chain reaction (PCR) and traditional cloning procedures such as those used to clone the human growth hormone gene?

A) PCR and traditional cloning make use of different types of bacteria. B) PCR and traditional cloning make use of different types of vectors. C) PCR uses plasmid vectors, whereas traditional cloning uses bacteria. D) PCR eliminates the need for restriction enzymes, vectors, and cells. E) PCR is more time-consuming, but the purity of the obtained DNA clone is much higher than in traditional cloning.

Biology & Microbiology

Olfaction is the sense of

A. smell. B. hearing. C. taste. D. vision. E. touch.

Biology & Microbiology

________ is directional growth responses of plants to a unidirectional source of light.

A. Phototropism B. Thermotropism C. Dormancy D. Thigmotropism E. Gravitropism

Biology & Microbiology

What is equational division

Fill in the blank(s) with the appropriate word(s).

Biology & Microbiology